1 Clinical Trials

1.3 Trial Objectives and Endpoints

Endpoints are the quantitative measurements implied or required by the trial objectives.

An endpoint is determined in each study subject, whereas the objectives are met by the aggregate of endpoints.”

Piantadosi (1997), p 127

For example

  • Asthma trial

  • objective: “reduced rate of treatment related adverse events such as asthma attacks”

  • endpoint:
    number of attacks suffered?
    (In what time-frame? How diagnosed? How/when followed-up?)

Endpoints: “hard” vs. “soft”

  • “hard” preferred:

    • well defined and reliable

    • no subjectivity: objectively measured

    • examples: death, presence of ulceration, laboratory measurements (e.g blood pressure, serum cholesterol, weight etc)

  • “soft”

    • difficult to define

    • subjective measures

    • examples: degree pf satisfaction with treatment, amount of pain (Visual Analogue Scales, VAS), severity of depression (numerical score: 0 - 10, MADRS, HAMD etc.)